| Preface to Cooley's Anemia: Ninth Symposium |
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| Clinical trials in thalassemia: insights from the patient community |
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Pathogenesis and management of iron toxicity in thalassemia |
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1 | (9) |
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The role of antioxidants and iron chelators in the treatment of oxidative stress in thalassemia |
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10 | (7) |
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Thalassemia as a global health problem: recent progress toward its control in the developing countries |
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17 | (7) |
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Iron metabolism and ineffective erythropoiesis in β-thalassemia mouse models |
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24 | (7) |
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Hepcidin in β-thalassemia |
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31 | (5) |
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Therapy for β-globinopathies: a brief review and determinants for successful and safe correction |
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36 | (9) |
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Humanized mouse models of Cooley's anemia: correct fetal-to-adult hemoglobin switching, disease onset, and disease pathology |
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45 | (7) |
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Strategy for a multicenter phase I clinical trial to evaluate globin gene transfer in β-thalassemia |
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52 | (7) |
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Hematopoietic stem cell mobilization strategies for gene therapy of beta thalassemia and sickle cell disease |
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59 | (5) |
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George Stamatoyannopoulos |
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Transcriptional silencing of fetal hemoglobin by BCL11A |
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64 | (5) |
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The challenge of obtaining therapeutic levels of genetically modified hematopoietic stem cells in β-thalassemia patients |
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69 | (6) |
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75 | (4) |
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Combined iron chelation therapy |
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79 | (8) |
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Deferasirox---current knowledge and future challenges |
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87 | (7) |
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Monitoring the efficiency of iron chelation therapy: the potential of nontransferrin-bound iron |
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94 | (6) |
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Critical appraisal of growth retardation and pubertal disturbances in thalassemia |
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100 | (15) |
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Magnetic resonance assessment of iron overload by separate measurement of tissue ferritin and hemosiderin iron |
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115 | (8) |
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Predicting pituitary iron and endocrine dysfunction |
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123 | (6) |
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Better survival and less cardiac morbidity in female patients with thalassemia major: a review of the literature |
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129 | (5) |
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A preclinical approach for gene therapy of β-thalassemia |
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134 | (7) |
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The role of reduced intensity preparative regimens in patients with thalassemia given hematopoietic transplantation |
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141 | (8) |
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Progress in hematopoietic stem cell transplantation as allogeneic cellular gene therapy in thalassemia |
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149 | (6) |
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Emerging insights in the management of hemoglobin E beta thalassemia |
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155 | (3) |
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Vivekanandan Thayalsuthan |
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Fetal globin gene inducers: novel agents and new potential |
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158 | (7) |
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Detection of the cardiovascular complications of thalassemia by echocardiography |
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165 | (8) |
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Cardiovascular MRI in thalassemia major |
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173 | (7) |
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Complexity of alpha thalassemia: growing health problem with new approaches to screening, diagnosis, and therapy |
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180 | (8) |
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Nutritional deficiencies in patients with thalassemia |
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188 | (9) |
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Ferritin iron minerals are chelator targets, antioxidants, and coated, dietary iron |
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197 | (8) |
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Pulmonary hypertension in thalassemia |
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205 | (9) |
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The natural history of thalassemia intermedia |
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214 | (7) |
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Hepcidin and Hfe in iron overload in β-thalassemia |
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221 | (5) |
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Fertility potential in thalassemia major women: current findings and future diagnostic tools |
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226 | (5) |
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Redefining thalassemia as a hypercoagulable state |
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231 | (6) |
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Treatment options for thalassemia patients wtih osteoporosis |
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237 | (7) |
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Health care transition in thalassemia: pediatric to adult-oriented care |
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244 | (4) |
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Ninth Cooley's Anemia Symposium: summary and perspective |
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248 | |
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